Gene therapy for sickle cell disease passes key preclinical test — Harvard Gazette

A precision-engineered gene therapy virus, inserted into blood stem cells that are then transplanted, markedly reduced sickle-induced red-cell damage in mice with sickle cell disease, researchers from Dana-Farber/Boston Children’s Cancer and Blood Disorders Center reported in the Journal of Clinical Investigation.

Gene editing shows promise as sickle cell therapy — Harvard Gazette

PDF) Editing Human DNA Moral and social implications of germline genetic modification

December, 2016, The Stem Cellar

New gene therapy could provide cure for sickle cell disease

Денис Савин (@withoutpassions) / X

Health Archives — Page 34 of 107 — Harvard Gazette

Gene Therapies for Sickle Cell Disease: A Promise Yet to Reach the Neediest

New study shows promising evidence for sickle cell gene therapy - UChicago Medicine

A systematic review of quality of life in sickle cell disease and thalassemia after stem cell transplant or gene therapy - ScienceDirect

gene therapy, The Stem Cellar

Milwaukee Area Sickle Cell Support Group

Gene therapy for sickle cell disease passes key preclinical test — Harvard Gazette